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Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa.
Bischof J, March OP, Liemberger B, Haas SA, Hainzl S, Petković I, Leb-Reichl V, Illmer J, Korotchenko E, Klausegger A, Hoog A, Binder HM, Garcia M, Duarte B, Strunk D, Larcher F, Reichelt J, Guttmann-Gruber C, Wally V, Hofbauer JP, Bauer JW, Cathomen T, Kocher T, Koller U. Bischof J, et al. Among authors: cathomen t. Mol Ther. 2022 Aug 3;30(8):2680-2692. doi: 10.1016/j.ymthe.2022.04.020. Epub 2022 Apr 30. Mol Ther. 2022. PMID: 35490295 Free PMC article.
Therapeutic genome editing with engineered nucleases.
Haas SA, Dettmer V, Cathomen T. Haas SA, et al. Among authors: cathomen t. Hamostaseologie. 2017 Jan 31;37(1):45-52. doi: 10.5482/HAMO-16-09-0035. Epub 2017 Jan 10. Hamostaseologie. 2017. PMID: 28070592 Review.
Automated generation of gene-edited CAR T cells at clinical scale.
Alzubi J, Lock D, Rhiel M, Schmitz S, Wild S, Mussolino C, Hildenbeutel M, Brandes C, Rositzka J, Lennartz S, Haas SA, Chmielewski KO, Schaser T, Kaiser A, Cathomen T, Cornu TI. Alzubi J, et al. Among authors: cathomen t. Mol Ther Methods Clin Dev. 2020 Dec 25;20:379-388. doi: 10.1016/j.omtm.2020.12.008. eCollection 2021 Mar 12. Mol Ther Methods Clin Dev. 2020. PMID: 33575430 Free PMC article.
A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosa.
Kocher T, Bischof J, Haas SA, March OP, Liemberger B, Hainzl S, Illmer J, Hoog A, Muigg K, Binder HM, Klausegger A, Strunk D, Bauer JW, Cathomen T, Koller U. Kocher T, et al. Among authors: cathomen t. Mol Ther Nucleic Acids. 2021 May 29;25:237-250. doi: 10.1016/j.omtn.2021.05.015. eCollection 2021 Sep 3. Mol Ther Nucleic Acids. 2021. PMID: 34458008 Free PMC article.
153 results