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Page 1
Prevalence and Relevance of Pre-Existing Anti-Adeno-Associated Virus Immunity in the Context of Gene Therapy for Crigler-Najjar Syndrome.
Hum Gene Ther. 2019 Oct;30(10):1297-1305. doi: 10.1089/hum.2019.143.
Hum Gene Ther. 2019.
PMID: 31502485
Free PMC article.
Lentiviral gene therapy for X-linked chronic granulomatous disease.
Kohn DB, Booth C, Kang EM, Pai SY, Shaw KL, Santilli G, Armant M, Buckland KF, Choi U, De Ravin SS, Dorsey MJ, Kuo CY, Leon-Rico D, Rivat C, Izotova N, Gilmour K, Snell K, Dip JX, Darwish J, Morris EC, Terrazas D, Wang LD, Bauser CA, Paprotka T, Kuhns DB, Gregg J, Raymond HE, Everett JK, Honnet G, Biasco L, Newburger PE, Bushman FD, Grez M, Gaspar HB, Williams DA, Malech HL, Galy A, Thrasher AJ; Net4CGD consortium.
Kohn DB, et al. Among authors: honnet g.
Nat Med. 2020 Feb;26(2):200-206. doi: 10.1038/s41591-019-0735-5. Epub 2020 Jan 27.
Nat Med. 2020.
PMID: 31988463
Free PMC article.
Clinical Trial.
Item in Clipboard
Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome.
Hacein-Bey Abina S, Gaspar HB, Blondeau J, Caccavelli L, Charrier S, Buckland K, Picard C, Six E, Himoudi N, Gilmour K, McNicol AM, Hara H, Xu-Bayford J, Rivat C, Touzot F, Mavilio F, Lim A, Treluyer JM, Héritier S, Lefrère F, Magalon J, Pengue-Koyi I, Honnet G, Blanche S, Sherman EA, Male F, Berry C, Malani N, Bushman FD, Fischer A, Thrasher AJ, Galy A, Cavazzana M.
Hacein-Bey Abina S, et al. Among authors: honnet g.
JAMA. 2015 Apr 21;313(15):1550-63. doi: 10.1001/jama.2015.3253.
JAMA. 2015.
PMID: 25898053
Free PMC article.
Clinical Trial.
Item in Clipboard
A poxvirus vaccine is safe, induces T-cell responses, and decreases viral load in patients with chronic hepatitis C.
Habersetzer F, Honnet G, Bain C, Maynard-Muet M, Leroy V, Zarski JP, Feray C, Baumert TF, Bronowicki JP, Doffoël M, Trépo C, Agathon D, Toh ML, Baudin M, Bonnefoy JY, Limacher JM, Inchauspé G.
Habersetzer F, et al. Among authors: honnet g.
Gastroenterology. 2011 Sep;141(3):890-899.e1-4. doi: 10.1053/j.gastro.2011.06.009. Epub 2011 Jun 13.
Gastroenterology. 2011.
PMID: 21699798
Clinical Trial.
Item in Clipboard
Efficacy of immunotherapy with TG4040, peg-interferon, and ribavirin in a Phase 2 study of patients with chronic HCV infection.
Di Bisceglie AM, Janczweska-Kazek E, Habersetzer F, Mazur W, Stanciu C, Carreno V, Tanasescu C, Flisiak R, Romero-Gomez M, Fich A, Bataille V, Toh ML, Hennequi M, Zerr P, Honnet G, Inchauspé G, Agathon D, Limacher JM, Wedemeyer H.
Di Bisceglie AM, et al. Among authors: honnet g.
Gastroenterology. 2014 Jul;147(1):119-131.e3. doi: 10.1053/j.gastro.2014.03.007. Epub 2014 Mar 18.
Gastroenterology. 2014.
PMID: 24657484
Clinical Trial.
Item in Clipboard
Hepatitis C vaccine: supply and demand.
Inchauspé G, Honnet G, Bonnefoy JY, Nicosia A, Strickland GT.
Inchauspé G, et al. Among authors: honnet g.
Lancet Infect Dis. 2008 Dec;8(12):739-40. doi: 10.1016/S1473-3099(08)70266-4.
Lancet Infect Dis. 2008.
PMID: 19022189
No abstract available.
Item in Clipboard
[Which follow-up for innovative treatments?].
Campana-Salort E, Espil-Taris C, Prigent H, de Antonio M, Lebrun-Vignes B, Tiffreau V, Honnet G.
Campana-Salort E, et al. Among authors: honnet g.
Med Sci (Paris). 2019 Mar;35 Hors série n° 1:54-56. doi: 10.1051/medsci/2019053. Epub 2019 Apr 3.
Med Sci (Paris). 2019.
PMID: 30943166
Free article.
French.
No abstract available.
Item in Clipboard
216th ENMC international workshop: Clinical readiness in FKRP related myopathies January 15-17, 2016 Naarden, The Netherlands.
Richard I, Laurent JP, Cirak S, Vissing J; ENMC FKRP Study Group.
Richard I, et al.
Neuromuscul Disord. 2016 Oct;26(10):717-724. doi: 10.1016/j.nmd.2016.08.012. Epub 2016 Aug 24.
Neuromuscul Disord. 2016.
PMID: 27639504
No abstract available.
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