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Randomized, clinical trial of RT001: Early signals of efficacy in Friedreich's ataxia.
Mov Disord. 2018 Jul;33(6):1000-1005. doi: 10.1002/mds.27353. Epub 2018 Apr 6.
Mov Disord. 2018.
PMID: 29624723
Clinical Trial.
Strong correlations among four measures of disease progression in Friedreich's ataxia.
Saal HJ, Heerinckx F, Zawadzki R, Omidvar O, Kilpatrick M, Zesiewicz T.
Saal HJ, et al. Among authors: heerinckx f.
Mov Disord. 2018 Jul;33(6):1021-1022. doi: 10.1002/mds.27351. Epub 2018 Apr 6.
Mov Disord. 2018.
PMID: 29624733
No abstract available.
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Treatment of infantile neuroaxonal dystrophy with RT001: A di-deuterated ethyl ester of linoleic acid: Report of two cases.
Adams D, Midei M, Dastgir J, Flora C, Molinari RJ, Heerinckx F, Endemann S, Atwal P, Milner P, Shchepinov MS.
Adams D, et al. Among authors: heerinckx f.
JIMD Rep. 2020 Mar 27;54(1):54-60. doi: 10.1002/jmd2.12116. eCollection 2020 Jul.
JIMD Rep. 2020.
PMID: 32685351
Free PMC article.
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Plasma and Red Blood Cell Membrane Accretion and Pharmacokinetics of RT001 (bis-Allylic 11,11-D2-Linoleic Acid Ethyl Ester) during Long Term Dosing in Patients.
Brenna JT, James G, Midei M, Heerinckx F, Atwal P, Milner P, Schmidt K, van der Ploeg L, Fielding R, Shchepinov MS.
Brenna JT, et al. Among authors: heerinckx f.
J Pharm Sci. 2020 Nov;109(11):3496-3503. doi: 10.1016/j.xphs.2020.08.019. Epub 2020 Aug 29.
J Pharm Sci. 2020.
PMID: 32871154
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RT001 in Progressive Supranuclear Palsy-Clinical and In-Vitro Observations.
Angelova PR, Andruska KM, Midei MG, Barilani M, Atwal P, Tucher O, Milner P, Heerinckx F, Shchepinov MS.
Angelova PR, et al. Among authors: heerinckx f.
Antioxidants (Basel). 2021 Jun 25;10(7):1021. doi: 10.3390/antiox10071021.
Antioxidants (Basel). 2021.
PMID: 34202031
Free PMC article.
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The infantile neuroaxonal dystrophy rating scale (INAD-RS).
Atwal PS, Midei M, Adams D, Fay A, Heerinckx F, Milner P.
Atwal PS, et al. Among authors: heerinckx f.
Orphanet J Rare Dis. 2020 Jul 29;15(1):195. doi: 10.1186/s13023-020-01479-5.
Orphanet J Rare Dis. 2020.
PMID: 32727524
Free PMC article.
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Double blind trial of a deuterated form of linoleic acid (RT001) in Friedreich ataxia.
Lynch DR, Mathews KD, Perlman S, Zesiewicz T, Subramony S, Omidvar O, Vogel AP, Krtolica A, Litterman N, van der Ploeg L, Heerinckx F, Milner P, Midei M.
Lynch DR, et al. Among authors: heerinckx f.
J Neurol. 2023 Mar;270(3):1615-1623. doi: 10.1007/s00415-022-11501-4. Epub 2022 Dec 3.
J Neurol. 2023.
PMID: 36462055
Clinical Trial.
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