Rescue of severe infantile hypophosphatasia mice by AAV-mediated sustained expression of soluble alkaline phosphatase.
Matsumoto T, Miyake K, Yamamoto S, Orimo H, Miyake N, Odagaki Y, Adachi K, Iijima O, Narisawa S, Millán JL, Fukunaga Y, Shimada T.
Matsumoto T, et al. Among authors: miyake k, miyake n.
Hum Gene Ther. 2011 Nov;22(11):1355-64. doi: 10.1089/hum.2010.210. Epub 2011 Jun 8.
Hum Gene Ther. 2011.
PMID: 21388343
Free PMC article.