AAV-mediated gene therapy in Dystrophin-Dp71 deficient mouse leads to blood-retinal barrier restoration and oedema reabsorption.
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Hum Mol Genet. 2016 Jul 15;25(14):3070-3079. doi: 10.1093/hmg/ddw159. Epub 2016 Jun 10.
Hum Mol Genet. 2016.
PMID: 27288449