BlockmiR AONs as Site-Specific Therapeutic MBNL Modulation in Myotonic Dystrophy 2D and 3D Muscle Cells and HSALR Mice.
Overby SJ, Cerro-Herreros E, Espinosa-Espinosa J, González-Martínez I, Moreno N, Fernández-Costa JM, Balaguer-Trias J, Ramón-Azcón J, Pérez-Alonso M, Møller T, Llamusí B, Artero R.
Overby SJ, et al. Among authors: perez alonso m.
Pharmaceutics. 2023 Mar 31;15(4):1118. doi: 10.3390/pharmaceutics15041118.
Pharmaceutics. 2023.
PMID: 37111604
Free PMC article.