Utilizing real-world evidence to investigate treatments in alternating hemiplegia of childhood: Implications for future trials in rare disease

Eur J Paediatr Neurol. 2024 Mar:49:A1. doi: 10.1016/j.ejpn.2024.04.002. Epub 2024 Apr 6.

Author

Stéphane Auvin¹

Affiliation

¹ Université Paris Cité, INSERM NeuroDiderot, Paris, France; APHP, Robert Debré University Hospital, Pediatric Neurology Department, CRMR Epilepsies Rares, EpiCare Member, Paris, France; Institut Universitaire de France, (IUF), Paris, France; Service de Neurologie Pédiatrique, CHU Hôpital Robert Debré, 48, boulevard Sérurier, 75935, PARIS CEDEX 19, France. Electronic address: stephane.auvin@aphp.fr.

PMID: 38600015
DOI: 10.1016/j.ejpn.2024.04.002

No abstract available

Publication types

Editorial

MeSH terms

Child
Clinical Trials as Topic / methods
Hemiplegia*
Humans
Rare Diseases*

Supplementary concepts

Alternating hemiplegia of childhood