Acoramidis in Transthyretin Amyloid Cardiomyopathy
N Engl J Med
.
2024 Apr 11;390(14):1345-1346.
doi: 10.1056/NEJMc2401669.
Authors
Johan Verbeeck
1
,
Mickaël De Backer
2
,
Marc Buyse
3
Affiliations
1
Hasselt University, Hasselt, Belgium johan.verbeeck@uhasselt.be.
2
One2Treat, Mont-Saint-Guibert, Belgium.
3
International Drug Development Institute, Ottignies-Louvain-la-Neuve, Belgium.
PMID:
38598811
DOI:
10.1056/NEJMc2401669
No abstract available
Publication types
Letter
Comment
MeSH terms
Amyloid Neuropathies, Familial* / complications
Amyloid Neuropathies, Familial* / drug therapy
Amyloid Neuropathies, Familial* / genetics
Cardiomyopathies* / drug therapy
Humans
Prealbumin / genetics
Substances
Prealbumin