Strengthening health systems for access to gene therapy in rare genetic disorders
Mol Ther Methods Clin Dev
.
2024 Mar 13;32(2):101220.
doi: 10.1016/j.omtm.2024.101220.
eCollection 2024 Jun 13.
Authors
Sonal Bhatia
1
,
Yann Le Cam
2
,
Juan Carrion
3
,
Lauren Diamond
1
,
Paul Fennessy
4
,
Safiyya Gassman
1
,
Felix Gutzwiller
5
,
Stephen Kagan
1
,
Diana Pankevich
1
,
Jennifer Young Maloney
1
,
Nitin Mahadev
1
,
Martin Schulz
1
,
Durhane Wong-Rieger
6
,
Paolo Morgese
7
Affiliations
1
Pfizer, Inc., New York, NY, USA.
2
EURORDIS, Paris, France.
3
Aliber, Totana, Spain.
4
Paul Fennessy Advisory, Melbourne, VIC, Australia.
5
University of Zurich, Zurich, Switzerland.
6
Canadian Organization for Rare Disorders, Toronto, ON, Canada.
7
Alliance for Regenerative Medicine, Brussels, Belgium.
PMID:
38516694
PMCID:
PMC10951444
DOI:
10.1016/j.omtm.2024.101220
No abstract available
Publication types
News