Accessory oligos for neuronal delivery of therapeutic siRNAs for ALS

Mol Ther Nucleic Acids. 2024 Mar 13;35(2):102153. doi: 10.1016/j.omtn.2024.102153. eCollection 2024 Jun 11.
No abstract available

Keywords: ASO; ASO delivery; accessory oligonucleotides; amyotrophic lateral sclerosis; in vivo; siRNA.

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