Cationic cholesterol-dependent LNP delivery to lung stem cells, the liver, and heart

Proc Natl Acad Sci U S A. 2024 Mar 12;121(11):e2307801120. doi: 10.1073/pnas.2307801120. Epub 2024 Mar 4.

Abstract

Adding a cationic helper lipid to a lipid nanoparticle (LNP) can increase lung delivery and decrease liver delivery. However, it remains unclear whether charge-dependent tropism is universal or, alternatively, whether it depends on the component that is charged. Here, we report evidence that cationic cholesterol-dependent tropism can differ from cationic helper lipid-dependent tropism. By testing how 196 LNPs delivered mRNA to 22 cell types, we found that charged cholesterols led to a different lung:liver delivery ratio than charged helper lipids. We also found that combining cationic cholesterol with a cationic helper lipid led to mRNA delivery in the heart as well as several lung cell types, including stem cell-like populations. These data highlight the utility of exploring charge-dependent LNP tropism.

Keywords: LNP; barcoding; mRNA; nanoparticle; scRNA-seq.

MeSH terms

  • Cations
  • Cholesterol
  • Heart
  • Liver*
  • RNA, Messenger
  • Stem Cells*

Substances

  • Cations
  • Cholesterol
  • RNA, Messenger