Macrocyclic Dual-Locked "Turn-On" Drug for Selective and Traceless Release in Cancer Cells

Angew Chem Int Ed Engl. 2024 Apr 24;63(18):e202314143. doi: 10.1002/anie.202314143. Epub 2024 Mar 27.

Abstract

Drug safety and efficacy due to premature release into the bloodstream and poor biodistribution remains a problem despite seminal advances in this area. To circumvent these limitations, we report drug cyclization based on dynamic covalent linkages to devise a dual lock for the small-molecule anticancer drug, camptothecin (CPT). Drug activity is "locked" within the cyclic structure by the redox responsive disulfide and pH-responsive boronic acid-salicylhydroxamate and turns on only in the presence of acidic pH, reactive oxygen species and glutathione through traceless release. Notably, the dual-responsive CPT is more active (100-fold) than the non-cleavable (permanently closed) analogue. We further include a bioorthogonal handle in the backbone for functionalization to generate cyclic-locked, cell-targeting peptide- and protein-CPTs, for targeted delivery of the drug and traceless release in triple negative metastatic breast cancer cells to inhibit cell growth at low nanomolar concentrations.

Keywords: drug delivery; dual-responsive chemotherapeutics; macrocyclic drugs; traceless release.

MeSH terms

  • Antineoplastic Agents* / chemistry
  • Camptothecin / chemistry
  • Cell Line, Tumor
  • Drug Delivery Systems
  • Drug Liberation
  • Micelles
  • Nanoparticles* / chemistry
  • Neoplasms*
  • Proteins
  • Tissue Distribution

Substances

  • Camptothecin
  • Antineoplastic Agents
  • Micelles
  • Proteins