Landmark endorsement of a global registry: The European Medicines Agency (EMA) Committee for Medicinal Products for Human Use (CHMP), publicly endorses World Federation of Hemophilia Gene Therapy Registry as global standard

Haemophilia. 2024 Jan;30(1):232-235. doi: 10.1111/hae.14912. Epub 2023 Dec 18.

Authors

Barbara A Konkle¹, Flora Peyvandi², Donna Coffin³, Mayss Naccache³, Toong Youttananukorn³, Glenn F Pierce³; WFH Gene Therapy Registry Scientific Advisory Board¹

Affiliations

¹ Washington Center for Bleeding Disorders, University of Washington, Seattle, Washington, USA.
² International Society on Thrombosis and Hemostasis, Carrboro, North Carolina, USA.
³ World Federation of Hemophilia, Montreal, Quebec, Canada.

PMID: 38111095
DOI: 10.1111/hae.14912

No abstract available

Publication types

Letter

MeSH terms

Drug Approval
Europe
Hemophilia A* / drug therapy
Humans
Registries