Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy
N Engl J Med
.
2023 Dec 7;389(23):2210-2211.
doi: 10.1056/NEJMc2312288.
Author
Fahreddin Palaz
1
Affiliation
1
Massachusetts General Hospital, Boston, MA fpalaz@mgh.harvard.edu.
PMID:
38055267
DOI:
10.1056/NEJMc2312288
No abstract available
Publication types
Letter
Comment
MeSH terms
Humans
Muscular Dystrophy, Duchenne* / genetics
Muscular Dystrophy, Duchenne* / therapy
Patients