Spinal muscular atrophy: Should we prescribe approved drugs to cohorts of patients in which they are unproven?

Eur J Neurol. 2024 Feb;31(2):e16103. doi: 10.1111/ene.16103. Epub 2023 Oct 25.

Authors

Lorenzo Fontanelli¹, Giulia Di Rauso², Gabriele Bellini¹

Affiliations

¹ Department of Clinical and Experimental Medicine, Neurology Unit, University of Pisa, Pisa, Italy.
² Department of Biomedical, Metabolic and Neural Sciences, University of Modena and Reggio Emilia, Modena, Italy.

PMID: 37877676
DOI: 10.1111/ene.16103

No abstract available

Publication types

Letter

MeSH terms

Humans
Muscular Atrophy, Spinal* / drug therapy
Patients
Spinal Muscular Atrophies of Childhood*