Elexacaftor/Tezacaftor/Ivacaftor therapy in cystic fibrosis children previously CFSPID: Is it over-medicalization?

J Cyst Fibros. 2024 Mar;23(2):366-367. doi: 10.1016/j.jcf.2023.10.008. Epub 2023 Oct 13.
No abstract available

Publication types

  • Letter

MeSH terms

  • Aminophenols* / therapeutic use
  • Benzodioxoles* / therapeutic use
  • Child
  • Chloride Channel Agonists / therapeutic use
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Cystic Fibrosis* / drug therapy
  • Drug Combinations
  • Humans
  • Indoles* / therapeutic use
  • Pyrazoles* / therapeutic use
  • Pyridines* / therapeutic use
  • Pyrroles / therapeutic use
  • Pyrrolidines
  • Quinolines / therapeutic use
  • Quinolones* / therapeutic use

Substances

  • elexacaftor
  • tezacaftor
  • ivacaftor
  • elexacaftor, ivacaftor, tezacaftor drug combination