No abstract available
Keywords:
AAV; Factor VIII; factor IX; gene editing; gene therapy; hemophilia A; hemophilia B.
MeSH terms
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Dependovirus / genetics
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Factor IX / genetics
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Factor IX / therapeutic use
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Factor VIII / genetics
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Factor VIII / therapeutic use
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Genetic Therapy
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Genetic Vectors / genetics
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Hemophilia A* / genetics
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Hemophilia A* / therapy
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Hemophilia B* / genetics
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Hemophilia B* / therapy
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Humans