Looking to the future of gene therapy for hemophilia A and B

Expert Rev Hematol. 2023 Jul-Dec;16(11):807-809. doi: 10.1080/17474086.2023.2268279. Epub 2023 Nov 17.
No abstract available

Keywords: AAV; Factor VIII; factor IX; gene editing; gene therapy; hemophilia A; hemophilia B.

Publication types

  • Editorial

MeSH terms

  • Dependovirus / genetics
  • Factor IX / genetics
  • Factor IX / therapeutic use
  • Factor VIII / genetics
  • Factor VIII / therapeutic use
  • Genetic Therapy
  • Genetic Vectors / genetics
  • Hemophilia A* / genetics
  • Hemophilia A* / therapy
  • Hemophilia B* / genetics
  • Hemophilia B* / therapy
  • Humans

Substances

  • Factor IX
  • Factor VIII