Bone mineral density in adult patients with pyruvate kinase deficiency on long-term mitapivat treatment

Haematologica. 2024 Mar 1;109(3):963-967. doi: 10.3324/haematol.2023.282884.
No abstract available

MeSH terms

  • Adult
  • Anemia, Hemolytic, Congenital Nonspherocytic*
  • Bone Density
  • Humans
  • Piperazines*
  • Pyruvate Kinase / deficiency*
  • Pyruvate Metabolism, Inborn Errors*
  • Quinolines*

Substances

  • mitapivat
  • Piperazines
  • Pyruvate Kinase
  • Quinolines

Supplementary concepts

  • Pyruvate Kinase Deficiency of Red Cells

Grants and funding

Funding: This study was funded by Agios Pharmaceuticals, Inc.