CRISPR-Cas9-mediated exon skipping as a cardioprotective strategy in Duchenne muscular dystrophy
Mol Ther Methods Clin Dev
.
2023 Sep 4:30:500-501.
doi: 10.1016/j.omtm.2023.08.013.
eCollection 2023 Sep 14.
Authors
Harry Wilton-Clark
1
,
Toshifumi Yokota
1
Affiliation
1
Department of Medical Genetics, University of Alberta, Edmonton, AB, Canada.
PMID:
37693945
PMCID:
PMC10491811
DOI:
10.1016/j.omtm.2023.08.013
No abstract available
Publication types
News