Identification of a Self-Assembling Small-Molecule Cancer Vaccine Adjuvant with an Improved Toxicity Profile

J Med Chem. 2023 Sep 28;66(18):13266-13279. doi: 10.1021/acs.jmedchem.3c01252. Epub 2023 Sep 7.

Abstract

Protein or peptide cancer vaccines usually include immune potentiators, so-called adjuvants. However, it remains challenging to identify structurally simple, chemically accessible synthetic molecules that are effective and safe as vaccine adjuvant. Here, we present cholicamideβ (6), a self-assembling small-molecule vaccine adjuvant with an improved toxicity profile and proven efficacy in vivo. We demonstrate that cholicamideβ (6), which is less cytotoxic than its parent compound, forms virus-like particles to potently activate dendritic cells with the concomitant secretion of cytokines. When combined with a peptide antigen, cholicamideβ (6) potentiated the antigen presentation on dendritic cells to induce antigen-specific T cells. As a therapeutic cancer vaccine adjuvant in mice, a mixture of cholicamideβ (6) and a peptide antigen protected mice from the challenges of malignant cancer cells without overt toxicity. Cholicamideβ (6) may offer a translational opportunity as an unprecedented class of small-molecule cancer vaccine adjuvants.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adjuvants, Immunologic / chemistry
  • Adjuvants, Immunologic / pharmacology
  • Adjuvants, Pharmaceutic
  • Adjuvants, Vaccine
  • Animals
  • Cancer Vaccines* / therapeutic use
  • Dendritic Cells
  • Mice
  • Neoplasms*
  • Peptides
  • T-Lymphocytes
  • Vaccines, Subunit

Substances

  • Cancer Vaccines
  • Adjuvants, Vaccine
  • Adjuvants, Immunologic
  • Adjuvants, Pharmaceutic
  • Vaccines, Subunit
  • Peptides