Editorial:
Ex-vivo
and
in-vivo
genome engineering for metabolic and neurometabolic diseases
Front Genome Ed
.
2023 Jul 6:5:1248904.
doi: 10.3389/fgeed.2023.1248904.
eCollection 2023.
Authors
Pasqualina Colella
1
,
Vasco Meneghini
2
3
,
Guilherme Baldo
4
,
Natalia Gomez-Ospina
1
Affiliations
1
Department of Pediatrics, Stanford University, Stanford, CA, United States.
2
San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCCS San Raffaele Scientific Institute, Milan, Italy.
3
Vita-Salute San Raffaele University, Milan, Italy.
4
Clinical Hospital of Porto Alegre, Federal University of Rio Grande do Sul, Porto Alegre, Brazil.
PMID:
37484653
PMCID:
PMC10359423
DOI:
10.3389/fgeed.2023.1248904
No abstract available
Keywords:
HDR; HSPC; NHEJ; genome editing; liver; metabolic; neurometabolic; retina.
Publication types
Editorial