Size matters: Fighting repeat expansion size in fragile X syndrome using antisense oligonucleotides

Proc Natl Acad Sci U S A. 2023 Jul 25;120(30):e2309678120. doi: 10.1073/pnas.2309678120. Epub 2023 Jul 13.
No abstract available

MeSH terms

  • Fragile X Mental Retardation Protein / genetics
  • Fragile X Mental Retardation Protein / metabolism
  • Fragile X Syndrome* / genetics
  • Humans
  • Oligonucleotides, Antisense / genetics
  • Oligonucleotides, Antisense / therapeutic use
  • Trinucleotide Repeat Expansion / genetics
  • Trinucleotide Repeats

Substances

  • Oligonucleotides, Antisense
  • Fragile X Mental Retardation Protein