Gene therapy for spinal muscular atrophy
Arch Dis Child Educ Pract Ed
.
2023 Oct;108(5):347-350.
doi: 10.1136/archdischild-2023-325359.
Epub 2023 Jul 9.
Authors
Vasantha Lakshmi Gowda
1
,
Heinz Jungbluth
2
3
,
Elizabeth Wraige
2
Affiliations
1
Department of Paediatric Neurology, Evelina London Children's Hospital, London, UK vasantha.gowda@gstt.nhs.uk.
2
Department of Paediatric Neurology, Evelina London Children's Hospital, London, UK.
3
Randall Division for Cell and Molecular Biophysics, Muscle Signalling Section, King's College, London, UK.
PMID:
37423714
DOI:
10.1136/archdischild-2023-325359
No abstract available
Keywords:
Neurology; Paediatrics; Pharmacology; Therapeutics.
MeSH terms
Genetic Therapy
Humans
Muscular Atrophy, Spinal* / diagnosis
Muscular Atrophy, Spinal* / genetics
Muscular Atrophy, Spinal* / therapy