A Glimmer of Hope for an Orphan Disease

N Engl J Med. 2023 Jul 6;389(1):81-82. doi: 10.1056/NEJMe2304147. Epub 2023 Jun 22.

Author

Affiliation

¹ From the Clinical Hepatology Research Section, Liver Diseases Branch, National Institute of Diabetes and Digestive and Kidney Diseases of the National Institutes of Health, Bethesda, MD.

PMID: 37345865
DOI: 10.1056/NEJMe2304147

No abstract available

Publication types

Editorial

MeSH terms

Hope
Humans
Rare Diseases* / therapy