Editorial: Genome and transcriptome editing to understand and treat neuromuscular diseases

Front Genome Ed. 2023 Mar 14:5:1176699. doi: 10.3389/fgeed.2023.1176699. eCollection 2023.

Authors

Rika Maruyama¹, Alyson Fiorillo², Christopher Heier², Dongsheng Duan³, Toshifumi Yokota¹

Affiliations

¹ Department of Medical Genetics, University of Alberta Faculty of Medicine and Dentistry, Edmonton, AB, Canada.
² Center for Genetic Medicine Research, Children's National Hospital, Washington, DC, United States.
³ Department of Molecular Microbiology and Immunology, School of Medicine, The University of Missouri, Columbia, MO, United States.

No abstract available

Keywords: 5′UTR; Duchenne muscular dystrophy; GNE; SOD1; amyotrophic lateral sclerosis; antisense oligonucleotides; microRNA; shRNAs.

Publication types

Editorial