Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party
Bone Marrow Transplant. 2023 May;58(5):594-596.
doi: 10.1038/s41409-023-01918-4.
Epub 2023 Feb 14.
1 Children's Hematopoietic Stem Cell Transplant Unit, Great North Children's Hospital, Newcastle, UK.
2 Translational and Clinical Research Institute, Newcastle University, Newcastle, UK.
3 Sigmund Freud University, Vienna, Austria.
4 Willink Unit, St Mary's Hospital, Manchester, UK.
5 EBMT Leiden Study Unit, Leiden, the Netherlands.
6 Royal Manchester Children's Hospital, Manchester, UK.
7 Department of Bone Marrow Transplantation, Hadassah Hospital, Faculty of Medicine, Hebrew University of Jerusalem, Jerusalem, Israel.
8 CHU Grenoble Alpes, Université Grenoble Alpes, Grenoble, France.
9 Department of Paediatrics, St. Anna Children's Hospital, Medical University of Vienna, Vienna, Austria.
10 Schneider Children's Medical Center of Israel, Petach-Tikva, Israel.
11 Unit of Pediatric Hematology and Pediatric BMT, Gazi University School of Medicine, Ankara, Turkey.
12 Department of Pediatrics, University Medical Center Ulm, Ulm, Germany.
13 Department of Pediatric Oncology, Sahlgrenska University Hospital, Gothenburg i, Sweden.
14 Department of Pediatric Hematology and Oncology, Hospital Universitari Vall d'Hebron, Barcelona, Spain.
15 Pediatric Onco-Hematology Department, Nancy University Hospital, Université de Lorraine, Vandoeuvre-les-Nancy, France.
16 Department of Pediatrics, Hospital Universitario de Salamanca, Salamanca, Spain.
17 Niño Jesus Children's Hospital, Madrid, Spain.
18 La Timone Children's Hospital and Aix-Marseille University, Marseille, France.
19 Department of Pediatrics, University Medical Center, Utrecht, Utrecht, the Netherlands.
20 Princess Máxima Center for Pediatric Oncology, Utrecht, the Netherlands.
21 Department of Pediatrics, Jena University Hospital, Jena, Germany.
22 Dr. von Hauner University Children's Hospital, Ludwig-Maximilians-Universität, Munich, Germany.
23 Willem-Alexander Children's Hospital, Pediatric Stem Cell Transplantation program, Leiden University Medical Center, Leiden, the Netherlands.
24 Pediatric Hematology-Immunology and Rheumatology Unit, Necker-Enfants Malades Hospital, Assistance Publique-Hôpitaux de Paris (APHP), Paris, France.
25 Royal Manchester Children's Hospital, Manchester, UK. robert.wynn@mft.nhs.uk.