First hemophilia B gene therapy approved: More than two decades in the making

Mol Ther. 2023 Jan 4;31(1):1-2. doi: 10.1016/j.ymthe.2022.12.001. Epub 2022 Dec 16.
No abstract available

Publication types

  • Editorial

MeSH terms

  • Factor IX / genetics
  • Factor VIII / genetics
  • Genetic Therapy
  • Genetic Vectors
  • Hemophilia A* / genetics
  • Hemophilia A* / therapy
  • Hemophilia B* / genetics
  • Hemophilia B* / therapy
  • Humans

Substances

  • Factor VIII
  • Factor IX