A retrograde approach for liver gene transfer

Nicola Brunetti-Pierri; Paul Gissen

doi:10.1016/j.omtm.2022.11.002

A retrograde approach for liver gene transfer

Mol Ther Methods Clin Dev. 2022 Nov 25:27:488-490. doi: 10.1016/j.omtm.2022.11.002. eCollection 2022 Dec 8.

Authors

Nicola Brunetti-Pierri^{1

2

3}, Paul Gissen^{4

5

6}

Affiliations

¹ Telethon Institute of Genetics and Medicine, Pozzuoli, Italy.
² Department of Translational Medicine, Federico II University, Naples, Italy.
³ Scuola Superiore Meridionale (SSM, School of Advanced Studies), Genomics and Experimental Medicine Program, University of Naples Federico II, Naples, Italy.
⁴ Genetics and Genomic Medicine Department, Great Ormond Street Institute of Child Health, University College London, London, UK.
⁵ National Institute of Health Research, Great Ormond Street Biomedical Research Centre, London, UK.
⁶ Metabolic Medicine Department, Great Ormond Street Hospital for Children NHS Foundation Trust, London, UK.

No abstract available

Keywords: gene therapy; hydrodynamic injections; hydrodynamic retrograde intrabiliary injection; nonviral vectors; ornithine transcarbamylase deficiency.

Publication types

News