One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency
Genet Med
.
2022 Oct;24(10):2209.
doi: 10.1016/j.gim.2022.08.011.
Authors
George A Diaz
,
Simon A Jones
,
Maurizio Scarpa
,
Karl Eugen Mengel
,
Roberto Giugliani
,
Nathalie Guffon
,
Isabela Batsu
,
Patricia A Fraser
,
Jing Li
,
Qi Zhang
,
Catherine Ortemann-Renon
PMID:
36205749
PMCID:
PMC9829548
DOI:
10.1016/j.gim.2022.08.011
No abstract available
Publication types
Published Erratum