Experience of compassionate-use pegcetacoplan for paroxysmal nocturnal hemoglobinuria

Blood. 2023 Jan 5;141(1):116-120. doi: 10.1182/blood.2022017266.
No abstract available

MeSH terms

  • Hemoglobinuria
  • Hemoglobinuria, Paroxysmal* / drug therapy
  • Humans
  • Peptides, Cyclic

Substances

  • pegcetacoplan
  • Peptides, Cyclic