The first successful expanded compassionate use of Iptacopan in a patient with paroxysmal nocturnal hemoglobinuria
Ann Hematol
.
2022 Nov;101(11):2537-2539.
doi: 10.1007/s00277-022-04933-5.
Epub 2022 Aug 15.
Authors
Bing Han
1
,
Jiang Ji
1
,
Bo Zhang
1
,
Hua Bai
1
,
Daobin Zhou
1
,
Feng Feng
1
,
Yan Huang
1
,
Huijuan Zhu
1
,
Limeng Chen
1
,
Zhihong Wu
1
,
Xiuchun Jiang
1
,
Xuemei Li
1
,
Qing Jia
1
,
Qing Chang
1
,
Hui Pan
1
,
Hua Peng
1
,
Wenting Zheng
1
,
Hui Huang
1
,
Zheng Chen
1
,
Chen Yang
1
,
Miao Chen
1
,
Bin Du
1
,
Shuyang Zhang
2
Affiliations
1
Peking Union Medical College Hospital, Beijing, China.
2
Peking Union Medical College Hospital, Beijing, China. shuyangzhang103@nrdrs.org.
PMID:
35965286
PMCID:
PMC9376122
DOI:
10.1007/s00277-022-04933-5
No abstract available
Publication types
Letter
MeSH terms
Compassionate Use Trials
Hemoglobinuria, Paroxysmal* / drug therapy
Humans
Immunologic Factors
Substances
Immunologic Factors
Grants and funding
CIFMS 2021-1-I2M-003/Chinese Academy of Medical Sciences (CAMS) innovation fund for medical sciences
81970106/National Natural Science Foundation of China (NSFC)