How Should the Effects of CFTR Modulator Therapy on Cystic Fibrosis Lung Disease Be Monitored?

Am J Respir Crit Care Med. 2022 Aug 1;206(3):240-242. doi: 10.1164/rccm.202204-0730ED.
No abstract available

Publication types

  • Editorial
  • Comment

MeSH terms

  • Alleles
  • Aminophenols / therapeutic use
  • Benzodioxoles
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Cystic Fibrosis* / drug therapy
  • Cystic Fibrosis* / genetics
  • Cystic Fibrosis* / pathology
  • Humans
  • Indoles
  • Lung / pathology
  • Magnetic Resonance Imaging
  • Pyrazoles
  • Pyridines
  • Pyrrolidines
  • Quinolones

Substances

  • Aminophenols
  • Benzodioxoles
  • CFTR protein, human
  • Indoles
  • Pyrazoles
  • Pyridines
  • Pyrrolidines
  • Quinolones
  • tezacaftor
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • ivacaftor
  • elexacaftor