Two Diseases-One Preclinical Treatment Targeting Glycogen Synthesis

Neurotherapeutics. 2022 Apr;19(3):977-981. doi: 10.1007/s13311-022-01240-9. Epub 2022 Apr 22.
No abstract available

Keywords: AAV9; Adult polyglucosan body disease; Glycogen; Glycogen storage disease; Lafora disease; Neurodegeneration.

Publication types

  • Research Support, N.I.H., Extramural
  • Comment

MeSH terms

  • Glycogen*
  • Muscle, Skeletal*

Substances

  • Glycogen