Lost in translation-Challenges in drug development for inherited metabolic diseases

J Inherit Metab Dis. 2022 May;45(3):381-382. doi: 10.1002/jimd.12501. Epub 2022 Apr 7.

Authors

Robin H Lachmann¹, Marc C Patterson², Sandra Sirrs³

Affiliations

¹ University College London Hospitals, London, UK.
² Mayo Clinic Children's Center, Rochester, Minnesota, USA.
³ University of British Columbia, Vancouver, British Columbia, Canada.

PMID: 35373847
DOI: 10.1002/jimd.12501

No abstract available

Publication types

Editorial

MeSH terms

Drug Development
Humans
Metabolic Diseases* / drug therapy