Heal thyself: The promise of autologous hematopoietic stem cell gene therapy in neurometabolic disorders

Mol Ther. 2022 Apr 6;30(4):1353-1354. doi: 10.1016/j.ymthe.2022.03.006. Epub 2022 Mar 20.

Author

Rebecca C Ahrens-Nicklas¹

Affiliation

¹ Division of Human Genetics, The Children's Hospital of Philadelphia, Philadelphia, PA, USA; Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA, USA. Electronic address: ahrensnicklasr@email.chop.edu.

No abstract available

Publication types

Editorial

MeSH terms

Cell Differentiation
Genetic Therapy
Hematopoietic Stem Cells*
Wound Healing*

Grants and funding

K08 NS105865/NS/NINDS NIH HHS/United States