Efficacy and Safety of Gene Therapy for β-Thalassemia

N Engl J Med. 2022 Feb 3;386(5):488-490. doi: 10.1056/NEJMe2118580.

Author

Emmanuel Payen¹

Affiliation

¹ From the Division of Innovative Therapies, Infectious Diseases Models for Innovative Therapies Research Center and Unité Mixte de Recherche-1184, French Alternative Energies and Atomic Energy Commission Fontenay-aux-Roses, INSERM, Université Paris-Saclay, Fontenay-aux-Roses, France.

PMID: 35108475
DOI: 10.1056/NEJMe2118580

No abstract available

Publication types

Editorial
Comment

MeSH terms

Genetic Therapy
Humans
beta-Thalassemia* / genetics
beta-Thalassemia* / therapy