Family Driven Development of Treatments for Rare Pediatric Neurological Diseases

Clin Pharmacol Ther. 2022 Apr;111(4):736-739. doi: 10.1002/cpt.2507. Epub 2021 Dec 26.

Authors

Kevin Romer¹, Oralea Marquardt², Shari Ungerleider³

Affiliations

¹ Mathew Forbes Romer Foundation, Boca Raton, Florida, USA.
² National Tay-Sachs and Allied Diseases Association, Boston, Massachusetts, USA.
³ Evan Lee Ungerleider Foundation, Wayne, New Jersey, USA.

PMID: 34957559
DOI: 10.1002/cpt.2507

No abstract available

MeSH terms

Child
Humans
Nervous System Diseases* / drug therapy
Rare Diseases / drug therapy