Challenging times: Delivering gene therapies and an opportunity for shared learning

Br J Clin Pharmacol. 2022 May;88(5):2444-2446. doi: 10.1111/bcp.15125. Epub 2021 Nov 8.

Authors

Cormac Kennedy^{1

2}, Edel O'Dea², Derval Reidy², Jeremy Towns², Maria Pigott², David Kevans^{2

3}, Declan O'Rourke⁴, Martina Hennessy^{1

2}

Affiliations

¹ Department of Pharmacology and Therapeutics, Health Sciences Centre, Trinity College, Dublin, Ireland.
² Wellcome-HRB Clinical Research Facility, St James Hospital, Dublin, Ireland.
³ Department of Gastroenterology, St James Hospital, Dublin, Ireland.
⁴ Department of Neurology, Children's Health Ireland at Temple Street, Dublin, Ireland.

PMID: 34750854
DOI: 10.1111/bcp.15125

No abstract available

Keywords: Zolgensma®; drug delivery; gene therapy; spinal muscle atrophy.

Publication types

Letter

MeSH terms

Genetic Therapy
Humans
Interdisciplinary Placement*
Learning
Muscular Atrophy, Spinal* / genetics