NINDS launches network to develop treatments for ultra-rare neurological diseases

Nat Biotechnol. 2021 Dec;39(12):1497-1499. doi: 10.1038/s41587-021-01125-w.

Authors

Nina F Schor¹, Amir P Tamiz¹, Walter J Koroshetz¹; NINDS Ultra-Rare Gene-based Therapy (URGenT) Working Group; Ann-Marie Broome²

Collaborators

NINDS Ultra-Rare Gene-based Therapy (URGenT) Working Group:
Julia L Bachman, Chris Boshoff, Janice Cordell, Neel T Dhruv, Amelie Gubitz, Adam L Hartman, Genevieve E Lind, Codrin I Lungu, Jill A Morris, Glen H Nuckolls, Shantadurga Rajaram, Ranga Rangarajan, Rebecca A Roof, Mario H Skiadopoulos, Natalia Strunnikova, Ling M Wong, Clinton B Wright

Affiliations

¹ The National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD, USA.
² The National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, MD, USA. ann-marie.broome@nih.gov.

PMID: 34737446
DOI: 10.1038/s41587-021-01125-w

No abstract available

Publication types

Letter

MeSH terms

Humans
National Institute of Neurological Disorders and Stroke (U.S.)
Nervous System Diseases* / therapy
Rare Diseases / genetics
Rare Diseases / therapy
Stroke*
United States