No abstract available
MeSH terms
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Amyloid Neuropathies, Familial* / genetics
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Amyloid Neuropathies, Familial* / therapy
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CRISPR-Cas Systems
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Gene Editing*
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Humans
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RNA, Guide, CRISPR-Cas Systems
Substances
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RNA, Guide, CRISPR-Cas Systems
Supplementary concepts
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Amyloidosis, Hereditary, Transthyretin-Related