Reply to: The need for evidence-based treatment decisions in spinal muscular atrophy type 0
Ann Clin Transl Neurol
.
2021 Oct;8(10):2093.
doi: 10.1002/acn3.51458.
Epub 2021 Sep 21.
Authors
Eugenio Mercuri
1
2
,
Eloisa Tiberi
3
,
Simonetta Costa
3
,
Marika Pane
1
2
,
Francesca Priolo
3
,
Domenico Romeo
2
,
Roberto de Sanctis
1
,
Danilo Tiziano
4
,
Giorgio Conti
5
,
Giovanni Vento
3
Affiliations
1
Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
2
Pediatric Neurology, Università Cattolica del Sacro Cuore, Rome, Italy.
3
Neonatology Unit, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
4
Institute of Genetics, Università Cattolica del Sacro Cuore, Rome, Italy.
5
Pediatric Intensive Care Unit, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
PMID:
34546660
PMCID:
PMC8528451
DOI:
10.1002/acn3.51458
No abstract available
Publication types
Letter
Comment
MeSH terms
Humans
Muscular Atrophy, Spinal* / diagnosis
Muscular Atrophy, Spinal* / therapy