Abstract
Keywords:
base editor; gene therapy; genome editing; hypertrophic cardiomyopathy.
Publication types
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Research Support, Non-U.S. Gov't
MeSH terms
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Animals
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Cardiomyopathy, Hypertrophic / genetics
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Cardiomyopathy, Hypertrophic / therapy*
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Cells, Cultured
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Gene Editing / methods
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Genetic Therapy / methods*
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HEK293 Cells
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Humans
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Male
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Mice
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Mice, Inbred C57BL
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Mutation
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Myosin Heavy Chains / genetics*
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Myosin Heavy Chains / metabolism
Substances
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Myh6 protein, mouse
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Myosin Heavy Chains