Paradigm shift in the era of disease-modifying therapies for Spinal Muscular Atrophy type 1: respiratory challenges and opportunities

Sleep Med. 2021 Oct:86:113-115. doi: 10.1016/j.sleep.2021.06.022. Epub 2021 Jun 25.
No abstract available

Keywords: Noninvasive ventilation; Nusinersen; Pulmonary clearance; Spinal muscular atrophy; Zolgensma.

Publication types

  • Editorial

MeSH terms

  • Humans
  • Muscular Atrophy, Spinal* / therapy
  • Spinal Muscular Atrophies of Childhood* / therapy