Guidance on Gene Replacement Therapy in Spinal Muscular Atrophy: A Canadian Perspective

Affiliations

• ¹ McGill University, Pediatrics and Neurology Neurosurgery, Montreal Children's Hospital, Montréal, Quebec, Canada.
• ² Research Institute of the McGill University Health Centre, Centre for Outcomes Research & Evaluation, Montréal, Quebec, Canada.
• ³ University of Toronto, Division of Neurology, Department of Pediatrics, The Hospital for Sick Children, Toronto, Ontario, Canada.
• ⁴ The Hospital for Sick Children, Centre for Computational Medicine, Toronto, Ontario, Canada.
• ⁵ Children's Hospital of Eastern Ontario, Division of Neurology, Ottawa, Ontario, Canada.
• ⁶ Children's Hospital of Eastern Ontario Research Institute, Ottawa, Ontario, Canada.
• ⁷ University of Ottawa, Faculty of Medicine, Ottawa, Ontario, Canada.
• ⁸ The Hospital for Sick Children, Department of Paediatrics, Division of Neurology, Toronto, Ontario, Canada.
• ⁹ Department of Paediatrics, University of Toronto, Toronto, Ontario, Canada.
• ¹⁰ The Hospital for Sick Children, Division of Respiratory Medicine, Toronto, Ontario, Canada.
• ¹¹ University of Toronto, Toronto, Ontario, Canada.
• ¹² Centre intégré universitaire de santé et de services sociaux du Saguenay-Lac-Saint-Jean du Québec, Groupe de Recherche Interdisciplinaire sur les Maladies Neuromusculaires (GRIMN), Hôpital de Jonquière, Saguenay, Québec, Canada.
• ¹³ Université de Sherbrooke, Centre de recherche Charles-Le Moyne-Saguenay-Lac-Saint-Jean sur les innovations en santé (CRCSIS), Longueuil/Saguenay, Quebec, Canada.
• ¹⁴ Université de Sherbrooke, Faculté de médecine et des sciences de la santé, Sherbrooke, Quebec, Canada.
• ¹⁵ The University of British Columbia, Division of Pediatric Neurology, Department of Pediatrics, Vancouver, British Columbia, Canada.