Treatment with patisiran of a patient with hereditary transthyretin-mediated amyloidosis with stage 3 polyneuropathy

Muscle Nerve. 2021 Sep;64(3):E11-E13. doi: 10.1002/mus.27338. Epub 2021 Jun 9.

Authors

Lars H Müschen¹, Gudrun Körner¹, Stefan Gingele¹, Anja Hänselmann², Udo Bavendiek², Thomas Skripuletz¹

Affiliations

¹ Department of Neurology, Hannover Medical School, Hannover, Germany.
² Department of Cardiology and Angiology, Hannover Medical School, Hannover, Germany.

PMID: 34075597
DOI: 10.1002/mus.27338

No abstract available

Publication types

Case Reports
Letter
Research Support, Non-U.S. Gov't

MeSH terms

Aged
Amyloid Neuropathies, Familial / drug therapy*
Humans
Male
Polyneuropathies / drug therapy*
RNA, Small Interfering / therapeutic use*
Treatment Outcome

Substances

RNA, Small Interfering
patisiran

Supplementary concepts

Amyloidosis, Hereditary, Transthyretin-Related