Case report of a complicated neurologically manifesting acute porphyria treated successfully with Givosiran

J Neurol Sci. 2021 Mar 15:422:117334. doi: 10.1016/j.jns.2021.117334. Epub 2021 Jan 31.
No abstract available

Keywords: Acute axonal neuropathy; Acute intermittent porphyria; Cerebral vasospasm; Givosiran; Porphyria.

Publication types

  • Case Reports
  • Letter

MeSH terms

  • Acetylgalactosamine / analogs & derivatives
  • Humans
  • Porphyria, Acute Intermittent* / complications
  • Porphyria, Acute Intermittent* / drug therapy
  • Pyrrolidines

Substances

  • Pyrrolidines
  • Acetylgalactosamine
  • givosiran