Special Issue "Genetic Advances in Neuromuscular Disorders: From Gene Identification to Gene Therapy"

Genes (Basel). 2021 Feb 8;12(2):242. doi: 10.3390/genes12020242.

Abstract

Since the gene responsible for Duchenne muscular dystrophy was first described in 1987 [...].

Publication types

  • Editorial
  • Introductory Journal Article
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Genetic Therapy*
  • Humans
  • Muscular Dystrophy, Duchenne / diagnosis
  • Muscular Dystrophy, Duchenne / genetics*
  • Muscular Dystrophy, Duchenne / therapy
  • Neuromuscular Diseases / diagnosis
  • Neuromuscular Diseases / genetics*
  • Neuromuscular Diseases / therapy