Gene Therapy for Cystic Fibrosis: Lessons Learned and Paths Forward

Mol Ther. 2021 Feb 3;29(2):428-430. doi: 10.1016/j.ymthe.2021.01.010. Epub 2021 Jan 12.

Authors

Soon H Choi¹, John F Engelhardt²

Affiliations

¹ Department of Anatomy and Cell Biology, University of Iowa, Carver College of Medicine, Iowa City, IA 52242, USA.
² Department of Anatomy and Cell Biology, University of Iowa, Carver College of Medicine, Iowa City, IA 52242, USA. Electronic address: john-engelhardt@uiowa.edu.

No abstract available

Publication types

Review

MeSH terms

Cystic Fibrosis / genetics
Cystic Fibrosis / therapy*
Cystic Fibrosis Transmembrane Conductance Regulator / genetics
Genetic Therapy* / methods
Humans

Substances

Cystic Fibrosis Transmembrane Conductance Regulator

Grants and funding