Small molecule drugs in cystic fibrosis

Arch Dis Child Educ Pract Ed. 2022 Oct;107(5):379-382. doi: 10.1136/archdischild-2020-319009. Epub 2020 Nov 19.
No abstract available

Keywords: cystic fibrosis; genetics; pharmacology.

MeSH terms

  • Cystic Fibrosis* / drug therapy
  • Humans
  • Mutation