Genetic prion disease: opportunities for early therapeutic intervention with rigorous pre-symptomatic trials

Expert Opin Investig Drugs. 2020 Dec;29(12):1313-1316. doi: 10.1080/13543784.2020.1839048. Epub 2020 Nov 1.
No abstract available

Publication types

  • Editorial

MeSH terms

  • Animals
  • Humans
  • Mutation
  • Prion Diseases / drug therapy
  • Prion Diseases / genetics*
  • Prion Proteins / genetics*
  • Research Design

Substances

  • PRNP protein, human
  • Prion Proteins